general/orphan-drugs
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Pasireotide
Pharmaceutical drug
Acetohydroxamic acid
Enzyme inhibitor that inhibits urease
Afegostat
Chemical compound
Alglucosidase alfa
Enzyme replacement therapy drug
Amifampridine
Chemical compound
Arylsulfatase B
Mammalian protein found in Homo sapiens
Eculizumab
Pharmaceutical drug
Triheptanoin
Chemical compound
Iloprost
Pharmaceutical drug
Carboprost
Chemical compound
Plerixafor
Chemical compound
Omacetaxine mepesuccinate
Chemical compound